Future of Health Summit 2022

Accelerating Access to Lifesaving Treatments and Cures: Insights from FDA's Expedited Review Programs

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The Food and Drug Administration's (FDA) expedited review processes have been instrumental in making treatments available for individuals living with serious illnesses. Manufacturers of new medical products leverage the four expedited programs: (1) priority review; (2) accelerated approval; (3) fast-track, and (4) breakthrough therapy to accelerate drug development and review. While these programs have been undoubtedly successful in fulfilling the goals for which they were introduced, they also attract their fair share of scrutiny, especially the accelerated approval pathway. Over the years, several drugs approved under the accelerated approval pathway have proven controversial and called into question concerns about patient safety for failure of sponsors to complete post-approval confirmatory studies. A recent FDA drug approval decision thrust the approval pathway into the spotlight. This session will review the successes of the accelerated approval pathway for the patient community, reform efforts underway, and how stakeholders are balancing the utility of expedited approval programs with concerns raised about their effectiveness. 

    Moderator

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    Michael McCaughan

    Founder, Prevision Policy

    Speakers

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    Jeff Allen

    President and CEO, Friends of Cancer Research
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    Holly Fernandez Lynch , MBE

    Assistant Professor of Medical Ethics and Law, University of Pennsylvania
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    Frank Sasinowski

    Director, Hyman, Phelps & McNamara
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    Jamie Sullivan

    Senior Director of Policy, EveryLife Foundation for Rare Diseases